New method boosts blood-clotting for hemophiliacs
ATLANTA—Researchers say they've finally succeeded in treating hemophiliacs with gene therapy.
Some experts call it a long-awaited breakthrough. But it was only a small study involving six patients in London, and the therapy would have to be tested on many more hemophiliacs before it could be called a definite success.
Hemophilia is an inherited, potentially deadly condition in which people bleed too easily. The researchers hoped an infusion of new DNA would fix their genetic defect and help their blood clot better. It worked, and lasted for months.
Researchers at St. Jude Children's Research Hospital led the study. It was presented on Saturday at a medical conference in San Diego.